The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...

This study presents an optimized CRISPR-Cas12a system for large-scale genetic screening, revealing critical genes involved in lymphoma development and therapy.

With the addition of Casgevy, Children’s Hospital Los Angeles now offers two gene therapies for sickle cell, the first being Lyfgenia.

Establishment and robust expansion of human fetal brain organoids ... Cas12a represents the next generation of gene editing. Here, the authors present the generation and validation of a Cas12a ...

Learn more› By Erin Roberts and Ben Keough After considering new apps, we still think that Adobe Lightroom and Snapseed are the best choices for editing photos when you’re away from a desktop ...

New gene therapies could transform sickle cell treatment forever. A future without pain crises or hospitalizations may finally be within reach.

January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...

Learn more about whether Catalyst Pharmaceuticals, Inc. or CRISPR Therapeutics AG is a better investment based on AAII's A+ ...

The best hard drives for video editing will help you get through your workload more quickly and store masses of footage in one easy-to-access place. Below, we've hand-picked the best HDDs and SSDs to ...

BEAM’s pipeline of gene editing therapies is based on its proprietary ... with BEAM-101 led to a robust and durable increase in fetal hemoglobin of more than 60% and a reduction in sickle ...

In this installment of Rebelliously Curious, we delve into one of the most debated scientific advancements of our time: CRISPR gene-editing technology. Joining us is Neal Baer, M.D.—pediatrician, ...