Announcement coincides with WORLDSymposium™ presentation highlighting knockdown of GYS1 mRNA and protein in muscle, as well as favorable safety and ...

The Phase Ib trial is set to test a gene therapy designed to target a rare disorder that causes muscle and respiratory failure.

Trial aims to establish safety and provide proof of concept for GYS1 inhibition as promising new treatment strategy in patients with late-onset Pompe disease ...

Keloids are fibrotic scars that extend beyond the boundaries of the original wound, often causing physical disfigurement and emotional distress. These scars are driven by an overproduction of ...

In an exciting advancement for dermatological science, researchers have uncovered the pivotal role of vitamin D and the enzyme CYP24A1 in the ...

Oracle Chairman Larry Ellison highlighted the potential medical benefits of the investment, stating that AI could be used to detect cancers and customize mRNA vaccines to treat them within 48 hours.

The U.S. government has handed Moderna almost $600 million to accelerate its work on various bird flu vaccines as well as work on mRNA vaccines for other influenza strains with pandemic potential.

Messenger RNA (mRNA) vaccines offer an adaptable and scalable platform for cancer immunotherapy, requiring optimal design to elicit a robust and targeted immune response. Recent advancements in ...

The global fight against cancer is at a pivotal moment. A breakthrough in Russia promises to redefine cancer treatment, with the country announcing its first mRNA cancer vaccine. This revolutionary ...

This work shows that overactive glycogen synthase (GYS1), but not metabolic dysregulation or glycogen hyperphosphorylation ... In conjunction with the study of disease-related mRNA expression changes, ...