The small study in patients with a rare disorder that causes liver and lung damage showed the potential for precisely ...

For this particular study, the team created fat-like molecules to form a protective shell around the CRISPR system. The ...

UD researchers discover that differences in gene expression in fat could be the key to targeted obesity treatment. According ...

Zandy Forbes’ biotech company MeiraGTx has developed targeted gene therapy methods to treat more than just genetic disorders.

Gene editing has taken root in plant breeding, leading to numerous advances in plant-based foods. K-State scientists, for ...

Calidi Biotherapeutics Inc. has released promising preclinical results for its systemic Rtnova platform showing its ability ...

Researchers from Tel Aviv University utilized CRISPR to cut a single gene from cancer cells of head and neck tumors – and ...

BEAM-302 "has set the bar for efficacy in this space," William Blair analysts wrote in an investor note on Monday.

Jonathon Whitton, AuD, PhD, VP, auditory global program head, Regeneron, discusses regulatory challenges for DB-OTO, Regeneron’s AAV-based gene therapy for hearing loss.